Spinal muscular atrophy (SMA) is a genetic disease that affects mostly children, but comes in different forms. The severe neuromuscular disease affects a person’s ability to participate in daily life functions, like walking, eating, or even breathing.
In this video shared by FightSMA in 2010, Dr. Bob Leshner, a pediatric neurologist and neuromuscular clinician, talks about the different types of SMA, in particular, type 3 and type 4, and their treatment programs. “It’s possible that a better understanding of the type 3 and the type 4 patient, understanding why their disease is so much more benign … may provide additional windows of insight into future therapeutic strategies,” he says.
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