News

May 8, 2019May 10, 2019

#AANAM – Interim Results from Phase 2 Trial of Spinraza in Infants with SMA Support Efficacy, Safety

News

Spinal muscular atrophy (SMA) treatment with Biogen’s Spinraza (nusinersen) has resulted in motor milestone achievements in line with normal motor development and continues to provide benefit to infants who began receiving ... Read more

May 8, 2019May 10, 2019

#AANAM – Spinraza Continues to Demonstrate Safety and Provide Improvements in SMA Patients

News

Treatment with Spinraza (nusinersen) results in greater improvements in motor function and continues to improve or stabilize motor function scores in spinal muscular atrophy (SMA) patients, according to recent ... Read more

May 6, 2019May 15, 2019

#AANAM – Rapid Motor Function Improvement with Zolgensma in Presymptomatic Infants with SMA Types 1-3, Early Trial Results Show

News

Treatment of presymptomatic babies with the investigational gene therapy Zolgensma provides rapid improvement in motor function in infants with spinal muscular atrophy (SMA) types 1, 2 and 3, according ... Read more

May 6, 2019May 7, 2019

#AANAM – Type 2 Patients Taking Well to Zolgensma, With Motor Milestones and No Safety Concerns

News

Type 2 patients with spinal muscular atrophy (SMA) given the gene therapy Zolgensma via spinal canal injection are showing no safety concerns so far and notable motor milestones, early results of a ... Read more

May 3, 2019May 3, 2019

Spinraza Found to Improve, Restore, Motor Function in Children with Late-Onset SMA in Long-term Trial

News

Long-term treatment with Biogen‘s Spinraza (nusinersen) showed clinically meaningful improvement in the motor function of children ages 2 to 15 with late-onset spinal muscular atrophy (SMA), trial data shows. Spinraza ... Read more

May 2, 2019May 2, 2019

From a ‘Gut-wrenching’ Diagnosis to a ‘Wonderful Drug’: Spinraza Users Share Their Stories in Biogen Webcast

News

Learning that spinal muscle atrophy was the reason her 15-month-old son couldn’t do what others his age could was a “gut-wrenching” moment, Kristen Farrell recalled in a recent webcast hosted ... Read more

May 1, 2019

PALS Uplifts the Spirits of Rare-Disease Patients by Offering Free Flights

News

Cumbersome security procedures, rising airfares, and shrinking legroom have made commercial air travel difficult enough these days — even for healthy passengers. Imagine how much harder it is for ... Read more

May 1, 2019May 1, 2019

SMA Patients in Saskatchewan, Canada, Gain Wider Access to Spinraza

News

The Canadian province of Saskatchewan has joined that of Quebec in granting access to Spinraza (nusinersen) therapy to a wider range of people with spinal muscular atrophy (SMA), Biogen Canada announced in a ... Read more

April 29, 2019April 29, 2019

High-intensity Training Improves Fitness While Being Safe for Patients with Kennedy’s Disease, Small Study Suggests

News

High-intensity training can improve fitness and may be performed safely by patients with spinal and bulbar muscular atrophy (SBMA), a small pilot study suggests. According to patients, high-intensity training (HIT) ... Read more

April 26, 2019April 26, 2019

Parents Need Supportive Care as Child Transitions to Wheelchair, Study Says

News

Parents of children with neuromuscular diseases who are prescribed wheelchair use should be involved in this process and receive psychological care and social support to facilitate transition to wheelchair equipment, according to a ... Read more

Pin It on Pinterest