Hi all! Please do share your thoughts about this first gene therapy for SMA.
Are you hoping to use it soon? Are you talking with your doctors about Zolgensma?
Do you think it will be approved for older patients with types 2 and 3 this year? Next year?
Or, because it’s only now only being tested in type 2 children up to age 5 (STRONG trial), do…[Read more]