Throughout 2017, SMA News Today has brought you daily coverage of spinal muscular atrophy (SMA)-related advocacy events, clinical studies and research updates. These were the top 10 SMA news stories ... Read more
The gene therapy developer AveXis will start a pivotal clinical trial of AVXS-101 for people with SMA type 1.
U.S. Food and Drug Administration officials agreed to the trial after AveXis submitted information the ... Read more
In the United Kingdom, the SMA Trust is working to promote research and development of new treatments for spinal muscular atrophy (SMA). By providing funding and bringing together researchers, ... Read more
In this video from Neurology Today, Dr. Brent Fogel, an associate professor of neurology and human genetics at the University of California, Los Angeles discusses two different types of treatment ... Read more