A new molecular compound, called LDN-2014, increases and stabilizes the levels of the survival motor neuron (SMN) protein, improving clinical outcomes in mouse models of mild and severe forms of spinal muscular ... Read more
Decreased levels of an enzyme lead to cellular dysfunction and neuronal degeneration involved in the development of spinal muscular atrophy (SMA), a new mouse study suggests. The study, “Neuronal activity regulates DROSHA ... Read more
Administering stem cell therapy to the fetuses of mice with spinal muscular atrophy (SMA) type 3 improved the animals’ movement and survival after birth, a study reports. The research, “Prenatal transplantation of ... Read more
The amount of a protein in small liquid-filled sacs that cells release could become a biomarker for spinal muscular atrophy, according to a study.
That’s because the levels of the survival ... Read more