treatment development

January 8, 2018July 12, 2018

FDA Lets AveXis Know the Information It Needs to Possibly Approve AVXS-101 for SMA Type 1

News

The U.S. Food and Drug Administration has given AveXis a list of information it needs to consider approving AVXS-101 as a treatment for spinal muscular atrophy Type 1. Company officials met with ... Read more

November 1, 2017November 2, 2017

Achievements, Hopes and Limits of SMA Treatment: Interview with Spinraza Researcher and CureSMA

News

Children with spinal muscular atrophy (SMA) type 1, who likely would have died before age 2 only a few years back, were seen to walk after being treated with ... Read more

June 15, 2017

UK’s SMA Trust Determined to Fund Research, Bring New Treatments to Patients

News

In the United Kingdom, the SMA Trust is working to promote research and development of new treatments for spinal muscular atrophy (SMA). By providing funding and bringing together researchers, ... Read more

December 15, 2016December 22, 2016

Steps Taken by Stem Cells in Becoming Neurons Identified in Study, Aiding Cell Replacement Therapies

News

Researchers have become quite good at making stem cells grow into neurons in the lab, even without fully understanding the actual cellular processes that accompany the transition. Now, a study describes ... Read more

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