[TIARA]

Hi Alyssa,

Thank you so much for taking the time to respond and for sharing this information. I truly appreciate it.

I will definitely reach out to the Boston Children’s Hospital SMA Program to see if they may be able to guide us regarding international patients or possible pathways for treatment.

Thank you again for your kindness and support.

[TIARA]

Hi Kevin,

Thank you very much for your response and for taking the time to guide me.

I have already reached out to Cure SMA and received an initial response. I am continuing to follow up with them and hoping they may be able to guide us further or connect us with additional resources.

I truly appreciate your support and recommendation. Thank you again.

[TIARA]

Hello everyone,

Just following up in case anyone has experience with early or managed access programs for SMA Type 1, or international pathways for Zolgensma.

Any guidance or even a small direction would mean a lot to our family.

Thank you again for your time.