• My First Mistake of 2018
  • AveXis Expands Clinical Testing of Gene Therapy, AVXS-101, to Include Milder SMA Types
  • How I Turned Terror into Triumph
  • Balancing Act
  • Polish City of Krakow to Host Europe’s First SMA Scientific Meeting Jan. 25-27
  • I’m Adaptable
  • Cure SMA Awards $450,000 to U.S. Care Centers, Creates Advocacy Action Network
  • Combining Two New Antisense Oligonucleotides Increases SMN Protein Levels in SMA Mice, Study Shows
  • The Good, the Bad, the Ugly, and the Beautiful
  • Shining Siblings
  • Spinraza Approved in Korea for SMA Treatment, Biogen Announces
  • My Latest Project for BioNews