• Patiently Waiting for an Itch to Be Scratched
  • #CureSMA2018 – Cytokinetics and Cure SMA Renew Partnership to Expand Education, Awareness
  • #CureSMA2018 – Science and Families at Center of Next Month’s Cure SMA Conference
  • #ERDC2018 – New EU Law to Protect Patient Data Could Affect Rare Disease Registries
  • Looking Back and Looking Forward
  • When the Impossible Becomes Possible
  • #CureSMA 2018 – Results of Phase 2 Test of Reldesemtiv in 70 SMA Patients Set for Release at Meeting
  • My College Experience: A Snapshot of the Good Old Days
  • Australia Adds Spinraza to Subsidized Coverage for SMA Kids, But Malaysia Still Waiting
  • Keep Your Hobbies Alive — You’d Regret Losing Them
  • ‘Rare Impact Awards’ Dinner Marks Orphan Drug Act and NORD at 35
  • Patients with SMA Types 2 and 3 at Risk of Malnutrition, Altered Metabolism, Study Reports