Make the Most Out of Your Time – Lockdown Tips
Our Forums moderator Kevin Schaefer published his list of entertainment options, perfect for these odd times we’re facing. To…
Articles by Isaura Santos
Isis Pharmaceuticals Receives $2.15M To Advance ISIS-SMN Rx In Children With SMA
Isis Pharmaceuticals recently announced it received $2.15 million from Biogen to advance CHERISH, the ongoing pivotal Phase 3 study assessing ISIS-SMNRx in children…
Isis Pharmaceuticals Reports Data On Spinal Muscular Atrophy
Isis Pharmaceuticals, Inc. recently revealed its latest data on the Phase 2, open-label and multiple-dose study of ISIS-SMNRx in children diagnosed with…
Cure SMA Awards $140,000 To Francesco Lotti From Columbia University
Francesco Lotti (https://www.curesma.org/news/grant-francesco-lotti.html) Francesco Lotti, PhD from Columbia University was recently awarded $140,000 in funding from Cure SMA to…
FightSMA and Gwendolyn Strong Foundation Announce Barrington G. Burnett As The $62,500 Emerging Investigator Award Winner
Dr. Barrington G. Burnett was named the recipient of the 2014 Emerging Investigator $62,500 Finalist Award, according to a recent …
AveXis Secures New Financing to Further SMA Clinical Studies
AveXis, Inc., a drug development company currently using gene therapy to address patients’ unmet needs suffering with orphan…
Dosing Completed For First Cohort in Type 1 Spinal Muscular Atrophy Clinical Trial
Orphan drug development company AveXis Inc. recently announced the completion of the dosing phase in the low-dose cohort of the company’s…