The Canadian Institutes for Health Research, a federal government agency based in Ottawa, has awarded genetics professor Kessen Patten C$627,300 to…
Articles by Janet Stewart, MSc
AveXis is working with the U.S. Food and Drug Administration (FDA) to overcome final regulatory hurdles before starting a…
A crucial two-hour meeting between AveXis executives and officials of the U.S. Food and Drug Administration (FDA) will determine the next step for AVXS-101,…
Spinraza (nusinersen), a treatment for most forms of spinal muscular atrophy (SMA), took a major step forward to…
A meeting that the spinal muscular atrophy (SMA) community is having with Food and Drug Administration officials in the Washington area…
In a recent webinar on Spinraza, the first approved treatment for spinal muscular atrophy (SMA), the patient advocacy group Cure SMA addressed…