Wheelchair Hockey Linked to Physical, Psychological Gains in Men
Playing wheelchair hockey is associated with better psychological well-being, self-perception of physical abilities, and quality of life in men with…
Articles by Marta Figueiredo, PhD
Team Behind Evrysdi Win 2 Prestigious ‘Drug Discovery’ Awards
The team of researchers who discovered and developed Evrysdi (risdiplam) — the first at-home oral therapy for spinal muscular atrophy…
Scholar Rock Shares Design of Phase 3 SAPPHIRE Trial of Apitegromab
Scholar Rock announced the full design of the upcoming Phase 3 clinical trial testing apitegromab, its experimental muscle-directed therapy…
Evrysdi May Be Available in Early 2022 to Eligible Patients in UK
The National Institute for Health and Care Excellence (NICE) has recommended that Roche’s Evrysdi (risdiplam) be covered by England’s…
Neurofilaments, Nerve-muscle Test Reflect SMA Severity in Very Young
The blood levels of neurofilaments — a marker of nerve cell damage — and the results of a nerve-muscle test…
Warning of Acute Liver Failure Added to Zolgensma Label
The U.S. Food and Drug Administration (FDA) has added acute liver failure to the list of safety concerns with use…
Ideal Therapy Aids Motor Skills and Breathing, Taken Orally: UK Survey
Motor function and stabilizing or improving breathing — along with oral administration — are the factors that adult patients and…
Neurofilament Blood Levels Likely to Predict Treatment Response in SMA
In infants with spinal muscular atrophy (SMA) type 1, lower blood levels of phosphorylated neurofilament heavy chain (pNF-H) —…
Spinraza RESPOND Trial Enrolling Children Not Helped by Zolgensma
Biogen is continuing to actively recruit patients for its Phase 4 RESPOND trial, which is evaluating the benefits of…
Blood NfL Levels May Mark SMA Severity, Therapy Efficacy in Very Young
Blood levels of neurofilament light chain (NfL) — a marker of nerve cell damage — in children and adolescents with…