Evrysdi (risdiplam) is an oral liquid treatment approved in the U.S. for infants through adults with spinal muscular atrophy (SMA) — patients age 2 months and older with any disease ... Read more
Spinal muscular atrophy (SMA) is a rare genetic disease with several subtypes. Patients and their caregivers may have a difficult time finding reliable information about SMA, so here are some ... Read more