News

Cure SMA Launches National Newborn Screening Campaign

The national nonprofit spinal muscular atrophy (SMA) support and advocacy organization Cure SMA has launched a grassroots campaign to have required newborn-screening for SMA in every state. The campaign was announced at the 2017 Annual SMA Conference held June 29-July 2 in Orlando, Florida. It was attended…

Cytokinetics Shares Baseline Characteristics of the First SMA Patients Enrolled in Phase 2 Trial Testing CK-2127107

Cytokinetics revealed preliminary data on the characteristics of patients with spinal muscular atrophy (SMA) screened for a Phase 2 trial to investigate the safety, tolerability and pharmacokinetics of CK-2127107. Data were presented by Cytokinetics’ director of clinical research, Stacy Rudnicki, MD, at the Cure SMA 2017 Annual SMA Conference in…

Spinraza Approved by Health Canada for Treating 5q SMA Patients

Spinraza (nusinersen) was just approved by Health Canada for the treatment of 5q spinal muscular atrophy (SMA) patients, Biogen Canada announced. This is the first therapy approved by Health Canada for the treatment of SMA. The drug is specifically indicated to treat 5q SMA, which represents about…