How long should I wait to see the results of Spinraza?

Written by Marta Figueiredo, PhD |

Category: Spinraza

Spinal muscular atrophy (SMA) is a progressive disease that can manifest in different ways, and treatment results will also vary. In a Phase 3 trial that tested the therapy in individuals with type 1 SMA, a severe form of the disease, about 41% of patients had attained new motor milestones after six months of treatment.