Which SMA treatment is most effective?

Written by Marta Figueiredo, PhD | Dec. 6, 2022

Which SMA treatment is most effective?

Category: SMA Treatment

To date, there is limited evidence from direct comparisons between disease-modifying therapies for spinal muscular atrophy (SMA). As such, no strong conclusions can be drawn about which treatment may be more effective. Evidence suggests that starting treatment early, especially prior to symptom onset, is more critical than DMT choice in achieving the best outcomes. SMA patients and/or their parents should talk to their healthcare team about eligibility for SMA treatments, and the potential risks and benefits of each therapy.

About the Author

Marta Figueiredo, PhD Marta holds a biology degree, a master’s in evolutionary and developmental biology, and a PhD in biomedical sciences from the University of Lisbon, Portugal. She was awarded a research scholarship and a PhD scholarship, and her research focused on the role of several signaling pathways in thymus and parathyroid glands embryonic development. She also previously worked as an assistant professor of an annual one-week embryology course at the University of Lisbon’s Faculty of Medicine.