Posts by: Ana de Barros, PhD

News

Risdiplam (RG7916) can improve both survival and motor function in patients with type 1 spinal muscular atrophy (SMA) beyond that expected in the natural history of the disease, according ... Read more

May 8, 2019May 8, 2019

#AANAM – Zolgensma Continues to Extend Survival in SMA Type 1 Patients Several Years After Dosing

News

A single administration of Zolgensma continues to extend the survival of patients with spinal muscular atrophy (SMA) type 1 while halting motor neuron loss several years after dosing, according to long-term ... Read more

June 8, 2018November 9, 2018

AveXis, Maker of SMA Therapy AVXS-101, Expanding Manufacturing Operations to North Carolina

News

AveXis is expanding its operations to North Carolina, opening up a new manufacturing center in Durham County, North Carolina Gov. Ray Cooper recently announced in a press release. The company ... Read more

June 1, 2018June 1, 2018

Envisagenics Awarded $1.5M to Refine SpliceCore, Platform Targeting Protein Production and Ways of Preventing Errors

News

Envisagenics announced that it has been given a two-year, $1.5 million grant from the National Institutes of Health (NIH) to further advance SpliceCore, a new biomarker and drug discovery platform. The ... Read more

May 30, 2018August 23, 2019

Biogen and Invitae Offering Free Genetic Testing for SMA to People in US

News

A program offered through a partnership between Invitae Corporation and Biogen offers free genetic testing to infants, children and others with clinically diagnosed spinal muscular atrophy or suspected of having the ... Read more

May 25, 2018May 25, 2018

#CureSMA2018 – Cytokinetics and Cure SMA Renew Partnership to Expand Education, Awareness

News

Cytokinetics and Cure SMA have expanded their existing partnership to increase education, awareness and fundraising for spinal muscular dystrophy (SMA). As a National Platinum Partner for 2018, Cytokinetics will ... Read more

May 2, 2018May 2, 2018

Canadian Institute Awarded $1.57M for New Research Facility to Study Motor Neuron Diseases

News

More than $1.57 million in funding, recently awarded to the Canadian Institut National de la Recherche Scientifique (INRS), will go toward new research facilities, including one to study motor ... Read more

March 28, 2018March 28, 2018

Genomic Vision Extends Collaboration with Quest Diagnostics to Improve SMA Diagnosis

News

Genomic Vision and Quest Diagnostics have agreed to extend their collaboration focusing on the potential development of new biomarkers to improve genetic diagnosis of spinal muscular atrophy. The partners will ... Read more

March 19, 2018March 19, 2018

Muscular Dystrophy Association to Expand Registry to Cover Seven Diseases

News

The Muscular Dystrophy Association (MDA) has asked the medical data services company IQVIA to expand its disease registry into a hub of information on seven neuromuscular conditions, including spinal muscular dystrophy (SMA). ... Read more

February 27, 2018March 1, 2018

NeuroNEXT Accelerates Research in SMA, Other Neurological Diseases

News

The National Network for Excellence in Neuroscience Clinical Trials is accelerating the clinical trial process for neurological diseases like spinal muscular atrophy with the expectation of bringing medications to ... Read more

Posts by: Ana de Barros, PhD

Ana de Barros, PhD

#AANAM – Risdiplam Improves Survival, Motor Function in Infants with Type 1 SMA, According to Data

#AANAM – Zolgensma Continues to Extend Survival in SMA Type 1 Patients Several Years After Dosing

AveXis, Maker of SMA Therapy AVXS-101, Expanding Manufacturing Operations to North Carolina

Envisagenics Awarded $1.5M to Refine SpliceCore, Platform Targeting Protein Production and Ways of Preventing Errors

Biogen and Invitae Offering Free Genetic Testing for SMA to People in US

#CureSMA2018 – Cytokinetics and Cure SMA Renew Partnership to Expand Education, Awareness

Canadian Institute Awarded $1.57M for New Research Facility to Study Motor Neuron Diseases

Genomic Vision Extends Collaboration with Quest Diagnostics to Improve SMA Diagnosis

Muscular Dystrophy Association to Expand Registry to Cover Seven Diseases

NeuroNEXT Accelerates Research in SMA, Other Neurological Diseases

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