Treatment with Evrysdi (risdiplam) improved motor function and quality of life in children and adults with spinal muscular…
Articles by Andrea Lobo
Far-field potentials (FFPs), electrical signals recorded with surface electrodes after nerve stimulation, may help track disease progression in people with…
A home-based respiratory physiotherapy program focused on breathing exercises and airway clearance techniques can significantly improve quality of life for…
Children with spinal muscular atrophy (SMA) showed trends suggesting that nutritional status may be linked to motor function, according…
Even when treated early with disease-modifying therapies (DMTs), infants and toddlers with spinal muscular atrophy (SMA) do not…
Genentech will not advance emugrobart (GYM329) into Phase 3 development, after early results from a clinical trial testing it…
Treatment with Spinraza (nusinersen) led to sustained improvements in motor function in adults with spinal muscular atrophy (SMA), and…
In children with spinal muscular atrophy (SMA) type 1, the most severe form of the genetic disease, treatment with…
Low levels of SMN protein in muscle stem cells (MuSC) — specialized cells that help sustain muscle growth and regeneration…
The blood creatinine-to-cystatin-c ratio (CCR), an indicator of muscle mass and strength, may be a biomarker of treatment response in…