Author Archives: Jose Marques Lopes PhD

Phase 1 Trial of AVXS-101 in SMA Type 2 Fully Enrolled

Patient enrollment is complete for AveXis’ Phase 1 clinical trial testing its gene therapy candidate AVXS-101 in patients with spinal muscular atrophy (SMA) type 2. “We are pleased that STRONG is now fully-enrolled and expect to report data from this study by May 2019,” David Lennon, PhD, the company’s president,…