Author Archives: Jose Marques Lopes PhD

Pre-symptomatic SMA Infants Show Stable Improvements in Respiratory, Motor Function in Spinraza Clinical Trial

All 25 pre-symptomatic infants treated with Biogen’s Spinraza (nusinersen) in a Phase 2 clinical trial of spinal muscular atrophy (SMA) did not require permanent ventilation and exhibited motor improvements, according to a preliminary analysis. The ongoing NURTURE study (NCT02386553) is assessing the effectiveness and safety of treatment…