#CureSMA2018 – Reldesemtiv Improves Muscle Strength in SMA Patients, Trial Data Show
Reldesemtiv improved muscle strength for walking and respiration in a dose-dependent manner in spinal muscular atrophy (SMA) patients, data…
Articles by Kara Elam
Impaired Mitochondrial Dynamics Play Role in SMA Pathology
The degeneration of spinal motor neurons in spinal muscular atrophy (SMA) may be the direct result of abnormal mitochondrial (energy source of…
Spinal Muscular Atrophy Study Points to Blood Vessel Defects
U.K. researchers funded by the SMA Trust have found that insufficient blood supply may well contribute to motor neuron loss in spinal…
SMA Drug Developer AveXis Forms AveXis EU as European Subsidiary
Dallas, Texas-based AveXis, Inc., a biotechnology company currently developing an experimental therapy for Spinal Muscular Atrophy (SMA) through the use of…
Challenging the Assumptions for Effective SMA Drug Administration
A study published by a team of researchers at the Cold Spring Harbor Laboratory (CSHL) suggests that a…