Clinical Development for SMA Treatments Reviewed at Annual Conference
Progress reports on six treatment options for spinal muscular atrophy (SMA), all currently in clinical trials, were spotlighted at the recent 2016 Annual…
Articles by Magdalena Kegel
Study Identifies 7 Genes Affecting SMA Severity, Onset in Mice
Researchers at the National Tsing Hua University in Taiwan discovered seven new genes affecting severity and time of onset of…
Potential for SMA Therapies in Stem Cells for Motor Neuron Acquisition
New knowledge in stem cell research may help scientists advance cell therapies for motor neuron diseases such as spinal muscular atrophy…
Motor Neurons in SMA Patients May Express Fewer Key Proteins
Motor neurons in spinal muscular atrophy (SMA) patients express fewer proteins associated with neuronal development than those in healthy individuals, according to…
Cure SMA Argues for Greater Patient Input in Drug Development Process at FDA Meeting
Cure SMA has urged the U.S. Food and Drug Administration (FDA) to ensure that user fee agreement funds are…
Potential SMA Therapy Ready for a First Clinical Test
Roche recently announced that a new investigational medicine for the treatment of spinal muscular atrophy (SMA) — RG7916 — will soon advance to its…
Spinal Muscular Atrophy Carriers Can be Detected Through Next Generation Sequencing Method
Researchers have developed a novel method for detecting carriers of spinal muscular atrophy (SMA) using next generation sequencing screening. The new…