Children and young adults with spinal muscular atrophy (SMA) types 2 and 3 continue to report improved or stabilized…
Articles by Marisa Wexler, MS
Most children with spinal muscular atrophy (SMA) who were presymptomatic and treated with Spinraza (nusinersen) in the NURTURE…
Babies born in the Canadian province of Saskatchewan will now be tested for spinal muscular atrophy (SMA) as part…
A man with spinal muscular atrophy (SMA) type 2 in Japan who lived until his 60s was found after…
Many prenatal genetic counselors are unfamiliar with important concepts related to spinal muscular atrophy (SMA) and its treatment, according…
The U.S. Food and Drug Administration (FDA) is giving priority review to a request that the oral therapy Evrysdi (risdiplam)…
Within the U.S., there is marked state-to-state variation in guidelines for whether Medicaid will cover Spinraza (nusinersen) or…
Biogen has exercised an option to acquire BIIB115, an investigational treatment for spinal muscular atrophy (SMA), from Ionis…
When it comes to treatments, people with spinal muscular atrophy (SMA) types 2 and 3 place a lot of…
Combined treatment with Spinraza and Zolgensma does not markedly improve motor function or breathing ability in children with spinal…