The U.S. Food and Drug Administration (FDA) has once again found problems at a manufacturing facility that was included on…
Articles by Marisa Horak, MS
In a few weeks, SMA News Today will host a free webinar exploring…
Registry studies can provide a valuable glimpse into how outcomes are evolving in rare diseases such as spinal muscular…
In infants diagnosed via newborn screening with spinal muscular atrophy (SMA), measures of nerve function may be a useful…
Different types of nerve cells respond differently when activity of a gene linked to spinal muscular atrophy (SMA) is reduced…
August is SMA Awareness Month, and advocates around the world are gearing up to raise awareness about spinal muscular…
A community-driven campaign called SMAshing My Limits And Going Places aims to make it easier for people with spinal…
An official decision on whether to approve apitegromab for spinal muscular atrophy (SMA) in the European Union may hinge…
England is rolling out newborn screening for spinal muscular atrophy (SMA), which will allow all babies born in the…
The spinal muscles of spinal muscular atrophy (SMA) patients who also have scoliosis show abnormalities in molecular activity, particularly in…