This Halloween, an 11-year-old living with spinal muscular atrophy (SMA) named Dash will be trick-or-treating in a costume fit for…
Articles by Marisa Horak, MS
Scholar Rock is working to bring spinal muscular atrophy (SMA) treatment Isembyld (apitegromab-mstn) to patients worldwide, following…
After its success in the U.S., Scholar Rock is once again seeking approval in the European Union for…
Activating a molecular recycling process called autophagy can improve motor function and extend lifespan in a nematode worm model of…
The brain has long been thought of as a singular organ, but a new study shows that the front and…
More than a year after the U.S. Food and Drug Administration (FDA) rejected the muscle-strengthening agent apitegromab for…
Managing a career, dating, and air travel for individuals with spinal muscular atrophy (SMA) comes down to three key…
The successful implementation of a spinal muscular atrophy (SMA) carrier screening program in southern China shows the “feasibility and…
In spinal muscular atrophy (SMA), the death of nerve cells — which results in the progressive muscle weakness and…
The U.S. Food and Drug Administration (FDA) has once again found problems at a manufacturing facility that was included on…