Too Little Known About Care Needs of Adults with SMA, Study Says
A better understanding of the needs of adults with spinal muscular atrophy (SMA), best ensuring for their mental and social…
Articles by Marisa Wexler, MS
Mom Writes of Family and Doctor ‘Partnership’ That Led to Baby’s Spinraza Treatment
A family’s journey through the diagnosis and treatment of their baby girl, born with spinal muscular atrophy type 1…
Taking Part in Adapted Sports Improves Mental Health, Study Finds
Among people with spinal muscular atrophy (SMA) and other neuromuscular disorders, participation in adapted sports is associated with greater…
Lack of Muscle Cell Signaling Seen to Kill Motor Neurons in SMA-LED2
Problems with the secretion of survival signals from muscle cells seems to be the dominant driver of motor neuron loss…
MDA Hosting Online Q&A on COVID-19 Today
The Muscular Dystrophy Association (MDA) is hosting an online Q&A session today to discuss the best ways that people…
Study Addresses Dilemmas Regarding Newborn Screening and SMA Treatment
As newborn screening for spinal muscular atrophy (SMA) becomes more common, ethical dilemmas will arise about the best treatment strategy…
Palliative Care has Improved for Babies With SMA Type 1, French Study Suggests
Palliative care for babies with spinal muscular atrophy (SMA) type 1 has improved in recent decades, with greater involvement…
Study Recommends Lower Radiation Dose for Spinraza Scans
Preforming an imaging scan that uses less radiation can be used to plan the administration of Spinraza (nusinersen) in…
Risdiplam Data to New Way of Classifying ‘Types’ Among SMA Europe 2020 Highlights, Advocate Says
Results from a clinical trial of risdiplam in a broad range of people with spinal muscular…
Cytokinetics and Cure SMA Renew Partnership
The biopharmaceutical company Cytokinetics and the nonprofit organization Cure SMA have announced a renewal of their partnership. The…