MDA Hosting Online Q&A on COVID-19 Today
The Muscular Dystrophy Association (MDA) is hosting an online Q&A session today to discuss the best ways that people…
Articles by Marisa Wexler, MS
Study Addresses Dilemmas Regarding Newborn Screening and SMA Treatment
As newborn screening for spinal muscular atrophy (SMA) becomes more common, ethical dilemmas will arise about the best treatment strategy…
Palliative Care has Improved for Babies With SMA Type 1, French Study Suggests
Palliative care for babies with spinal muscular atrophy (SMA) type 1 has improved in recent decades, with greater involvement…
Study Recommends Lower Radiation Dose for Spinraza Scans
Preforming an imaging scan that uses less radiation can be used to plan the administration of Spinraza (nusinersen) in…
Risdiplam Data to New Way of Classifying ‘Types’ Among SMA Europe 2020 Highlights, Advocate Says
Results from a clinical trial of risdiplam in a broad range of people with spinal muscular…
Cytokinetics and Cure SMA Renew Partnership
The biopharmaceutical company Cytokinetics and the nonprofit organization Cure SMA have announced a renewal of their partnership. The…
Zolgensma ‘Saved All of Our Lives’: A Family’s Journey Through Gene Therapy
Tina and Torence Anderson’s sixth and youngest child, Malachi, came into the world on July 31, 2015.
Rare Case of Severe SMA, Partly Evident by Bone Fractures at Birth, Reported in India
A child who barely moved in the womb in the final months before his birth and then had multiple bone…
‘I’ve Lived Through Death’ with SMA and ‘Through Life’ with Spinraza, Mom Says in Interview
Destiny McCalvin gave birth to her second child, a girl she named Kenzlee, after what she and her doctors took…
#AANAM – Spinraza Safe and Effective in Adults with SMA, Studies Suggest
Treating adults with spinal muscular atrophy (SMA) with Spinraza (nusinersen) was safe and improved their muscle strength,…