With about 100 spinal muscular atrophy (SMA) patients already treated with Zolgensma (onasemnogene abeparvovec-xioi) since the gene…
Articles by Mary Chapman
Some $6.6 million in new Muscular Dystrophy Association (MDA) multiyear grants will support promising studies in an array of…
Online forums have markedly altered how patients, caregivers, and healthcare professionals communicate and connect. Even when miles apart,…
SMA News Today, having launched forums and added regular columnists, is now running a month-long series to coincide with Spinal…
More than 90% of rare diseases have no federally sanctioned treatment. So when news came of an approved…
The Canadian province of Saskatchewan has joined that of Quebec in granting access to Spinraza (nusinersen) therapy to a wider range…
While the Canadian Association of Drugs and Technologies in Health (CADTH) recommended that the spinal muscular atrophy treatment Spinraza…
Spinraza (nusinersen) has been approved by China’s National Medical Product Administration (NMPA) for the treatment of the most common form…
Citing the deteriorating health of a child with spinal muscular atrophy (SMA), a member of the British Parliament is…
Scotland has joined the growing roster of countries making the spinal muscular atrophy (SMA) therapy Spinraza available to patients…