News

June 22, 2017

Cure SMA Pursues More Education and Better Clinical Trial Access, Capacity

News

Cure SMA announced the start of Phase 2 of its SMA Industry Collaboration, aiming to advance the development of specific goals. “The SMA Industry Collaboration is a multifaceted partnership ... Read more

June 21, 2017June 21, 2017

AveXis’ Gene Therapy AVXS-101 Edges Closer to Pivotal Trial for SMA Type 1

News

AveXis is working with the U.S. Food and Drug Administration (FDA) to overcome final regulatory hurdles before starting a pivotal trial of AVXS-101 for the treatment of spinal muscular ... Read more

June 15, 2017

UK’s SMA Trust Determined to Fund Research, Bring New Treatments to Patients

News

In the United Kingdom, the SMA Trust is working to promote research and development of new treatments for spinal muscular atrophy (SMA). By providing funding and bringing together researchers, ... Read more

June 13, 2017

Campaign to Persuade States to Screen Newborns for SMA to Be Key Topic at Conference

News

A revved-up campaign to persuade the U.S. government to ask states to screen newborns for spinal muscular atrophy will be a hallmark of this year’s SMA Conference in Orlando. The agenda ... Read more

June 8, 2017June 8, 2017

Anthem’s Insurance Policy for Spinraza Treatment Expands SMA Age Criteria

News

Anthem recently issued an updated insurance policy, expanding its coverage for the use of Spinraza (nusinersen), the first approved treatment for spinal muscular atrophy (SMA). The update revises the criteria for Spinraza in ... Read more

June 6, 2017June 6, 2017

Cure SMA Announces Presenters for Upcoming 2017 Family Friendly Poster Session

News

One way Cure SMA’s Annual SMA Conference encourages collaboration among academics, industry executives, government officials and families is through its Family Friendly Poster Session – a yearly event in which researchers ... Read more

June 1, 2017June 2, 2017

Spinraza Approved in Europe to Treat SMA Types 1-3

News

Spinal muscular atrophy (SMA) patients in the European Union will soon have access to Spinraza (nusinersen), the first treatment approved for people with this disease and one able to treat ... Read more

June 1, 2017

Ongoing Training for Family Caregivers of Ventilator-dependent Kids with SMA Improves Assistance

News

Continuous simulation training for family caregivers of children with spinal muscular atrophy (SMA) leads to improved assistance at home and better clinical outcomes, according to new research. The study, “An ... Read more

May 30, 2017May 30, 2017

Argentinian Receives Cure SMA Award to Research SMA Epigenetics

News

Alberto Kornblihtt, PhD, professor and group leader at the Universidad de Buenos Aires in Argentina, has been awarded a $140,000 grant for a project examining genetic changes that affect ... Read more

May 25, 2017May 25, 2017

Cure SMA Awards OSU’s Stephen J. Kolb $75,000 Grant to Study Motor Neuron Pathology in SMA Piglets

News

Cure SMA has awarded a $75,000 basic research grant to Dr. Stephen J. Kolb of Ohio State University (OSU) for a project that seeks a deeper understanding of motor neuron ... Read more