PTEN Depletion Found To Decrease Spinal Muscular Atrophy Disease Severity, Prolongs Survival Modestly in Animal Studies
Findings from a new study published in the journal Molecular Therapy offer a promising therapeutic strategy for patients with Spinal Muscular Atrophy (SMA). Spinal muscular atrophy (SMA) is an autosomal recessive disorder that causes loss of motor neurons and atrophy of the muscle, with patients presenting loss of…