Zolgensma ‘Saved All of Our Lives’: A Family’s Journey Through Gene Therapy
Tina and Torence Anderson’s sixth and youngest child, Malachi, came into the world on July 31, 2015.
Articles by Marisa Wexler, MS
Rare Case of Severe SMA, Partly Evident by Bone Fractures at Birth, Reported in India
A child who barely moved in the womb in the final months before his birth and then had multiple bone…
‘I’ve Lived Through Death’ with SMA and ‘Through Life’ with Spinraza, Mom Says in Interview
Destiny McCalvin gave birth to her second child, a girl she named Kenzlee, after what she and her doctors took…
#AANAM – Spinraza Safe and Effective in Adults with SMA, Studies Suggest
Treating adults with spinal muscular atrophy (SMA) with Spinraza (nusinersen) was safe and improved their muscle strength,…
#AANAM – Interim Results from Phase 2 Trial of Spinraza in Infants with SMA Support Efficacy, Safety
Spinal muscular atrophy (SMA) treatment with Biogen’s Spinraza (nusinersen) has resulted in motor milestone achievements in line with normal…
From a ‘Gut-wrenching’ Diagnosis to a ‘Wonderful Drug’: Spinraza Users Share Their Stories in Biogen Webcast
Learning that spinal muscle atrophy was the reason her 15-month-old son couldn’t do what others his age could was a…
ACTIVE Video Game Makes it More Fun for Patients to Monitor Their Motor Function
A video game called ACTIVE could be used to monitor changes in motor function in people with spinal muscular atrophy (SMA) types…
Study Highlights Difficulty of Transitioning from Pediatric to Adult Care for SMA Patients
Spinal muscular atrophy (SMA) patients transitioning from pediatric to adult care face unmet health needs and possible barriers to…
Protease Inhibitors Show Potential to Treat SMA By Raising SMN Protein Levels, Study Suggests
Through extensive experiments in cell and animal models of spinal muscular atrophy (SMA), investigators have demonstrated the possible usefulness of…
Recent Advancements in SMA Treatment, Screening Detailed in Review Study
Early intervention is crucial for the successful management of spinal muscular atrophy (SMA), according to the authors of a…