A new and noninvasive type of antisense oligonucleotide (ASO) therapy effectively treated spinal muscular atrophy (SMA) in a mouse…
Articles by Steve Bryson, PhD
Spinraza (nusinersen) improved fine manual dexterity — the ability to make coordinated finger movements to grasp and manipulate objects…
Delayed Spinraza (nusinersen) treatment due to the COVID-19 pandemic did not directly result in a worsening of symptoms in…
Genetic analysis of dried saliva spots identified people with spinal muscular atrophy (SMA), a study demonstrated and possibly for…
Tranexamic acid (TXA) effectively reduced blood loss by over 50% during surgery to correct for scoliosis caused by spinal…
For spinal muscular atrophy (SMA) patients with spinal deformities, administration of Spinraza (nusinersen) by a novel subcutaneous intrathecal…
School-age children and adolescents with spinal muscular atrophy (SMA) in China experience a high rate of anxiety and depression,…
In a letter to a U.S. Department of Transportation Advisory Committee, Cure SMA called for better wheelchair handling…
The Canadian Agency for Drugs and Technologies in Health (CADTH) will not recommend reimbursement for Zolgensma in children with…
Children with spinal muscular atrophy (SMA) type 2 or 3 in China have lower bone mineral density — putting…