Vishal K,  —

Rare Disease Day 2023

Recent Posts

• MDA 2023: Long-term motor gains seen for SMA children on Zolgensma
• Why I’m crowdfunding for the SMA treatment Evrysdi
• MDA 2023: Evrysdi’s motor benefits found to last for 4 years in trial
• Zolgensma gene therapy for SMA now routinely accessible in UK
• The truth about living with your middle-aged parents