Progress reports on six treatment options for spinal muscular atrophy (SMA), all currently in clinical trials, were recently spotlighted at the 2016 Annual SMA Conference in Anaheim, Calif. In this Nationwide Children’s Hospital video meet the Kingsley family and 6-year-old Brett who was diagnosed…
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Spinal Muscular Atrophy and the Genes Involved
Spinal muscular atrophy (SMA) is a genetic disease that affects mostly children. Sadly, some forms of SMA can lead to death. The severe neuromuscular disease causes the inability to participate in daily life functions like walking, eating, or even breathing. Read more about spinal muscular atrophy here. This disease is…
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What is SMA? Introduction to Spinal Muscular Atrophy
Spinal muscular atrophy (SMA) is a genetic disease that affects mostly children. Sadly, some forms of SMA can lead to death. The severe neuromuscular disease causes the inability to participate in daily life functions like walking, eating, or even breathing. Read more about spinal muscular atrophy here. In this video…
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