The Evolution of Adult Programs at the Cure SMA Conference
For many years, the annual Cure SMA Conference has been bringing the SMA community together to learn and to connect. Throughout its history, the conference has traveled to a variety of…
Cure SMA 2021
Read about some of the highlights of research presented at the SMA Research & Clinical Care Meeting, held June 9-11.
The Cure SMA Conference Reminded Me of the Strength in Community
This year marked the second entirely virtual annual Cure SMA conference. Instead of armies of wheelchair users invading Disneyland and hotels, we fellowshipped through virtual trivia nights…
#CureSMA2021 – Spinraza Leads to Better Swallowing, Farther Walking
Children with spinal muscular atrophy (SMA) who started taking Spinraza (nusinsersen) before symptoms appeared retained their ability to swallow after approximately four years, while youngsters with later-onset SMA walked farther with less…
#CureSMA2021 – Apitegromab Safely Increases Motor Abilities in SMA Types 2, 3
Meaningful further improvements in motor skills were evident with apitegromab treatment in later-onset spinal muscular atrophy (SMA) patients on maintenance doses of Spinraza (nusinersen), updated Phase 2 TOPAZ trial findings show. “The TOPAZ results show…
#CureSMA2021 – Evrysdi Linked to Improved Motor Function in 2 Trials
Evrysdi (risdiplam) continues to be linked to motor function improvements in a broad range of people with spinal muscular atrophy (SMA), according to recent data from two ongoing Phase 2 clinical trials.
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