• Patients, Supporters Worldwide Recognizing Rare Disease Day 2020
  • Living at Home as a Young Adult with SMA
  • SRK-015 Data Continue to Support Potential for SMA, Scholar Rock Says
  • Ella Shows Bravery After an Accident in Her Wheelchair
  • Risdiplam Data to New Way of Classifying ‘Types’ Among SMA Europe 2020 Highlights, Advocate Says
  • Risdiplam Use ‘Meaningful’ to Broadest SMA Group Ever in Clinical Trial, Genentech Exec Says
  • Learning to Navigate the World in My Permobil F3
  • Immediate Treatment Advised for Newborns with 4 Copies of SMN2 in Updated Guidelines
  • Peering Through the Fog of Fear
  • My Introduction to Death and Beyond
  • After Loss, Life Goes on for the Castens
  • 18 States in US Screening Newborns for SMA as Efforts Continue for More, MDA Says