In this Fight SMA annual webcast from 2014, a panel consisting of Dr. Chris Lorson, Dr. Elliot Androphy, Dr. Adrian Krainer, Dr. Charlotte Sumner, Dr. Brian Kaspar, Dr. John Porter, and Dr. Alex MacKenzie talk about the advances in the treatment of spinal muscular atrophy (SMA). The webcast was filmed in Washington DC at Fight SMA’s annual research conference.
The panel covers a broad range of topics including pre-clinical mouse model research for new medications for all types of SMA, stem cell therapy, clinical trials, FDA approval of new therapies, diet and supplements, and gene therapy.
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