Ahmad Kilo,  —

Articles by Ahmad Kilo

RaNA Therapeutics Presents Data Supporting Gene Upregulation as Spinal Muscular Atrophy Treatment

RaNA Therapeutics recently released preclinical data on its gene upregulation technology, which selectively triggers gene expression within cells, as a treatment for spinal muscular atrophy (SMA). The data were given in a poster presentation at the recent Keystone Symposium for Chromatin and Epigenetics in British Columbia, Canada. SMA, a major cause of infant mortality, results from mutations or deletions…

Thousands of Families Received Cure SMA Support and Resources in 2015

Cure SMA recently published a 2015 review of its advocacy work, highlighting the programs it provides to families living with Spinal Muscular Atrophy (SMA) that aid in caring for those with SMA and offering the emotional support of a unified community who understands the struggles of the disease. In its efforts to support the continued…

NIH Awards AMRI with 10-Year Contract for Neurologic Drug Development Services

Albany Molecular Research (AMRI), a contract research and manufacturing organization that provides drug discovery, development, cGMP manufacturing and aseptic fill and finish to the pharmaceutical and biotechnology industries, recently announced it has been granted a 10-year federal contract award care of the National Institutes of Health (NIH) to secure their drug development…

Roche Targets SMA With Acquisition of French Pharma Company

Swiss global health-care company Roche announced just last week that it has purchased Trophos, a privately-owned Marseille, France-based clinical stage pharmaceutical company that specializes in mitochondrial targeted compounds that work to improve the function and survival of stressed cells by preventing mitochondrial permeability transition, hence helping prevent cell death. Roche has taken an interest in…