Treatment with Spinraza (nusinersen) led to improvements in motor function for nearly all children with spinal muscular atrophy…
Articles by Marisa Wexler, MS
People with spinal muscular atrophy (SMA) who are treated with Spinraza (nusinersen) are less likely to require hospitalization…
Many adults with spinal muscular atrophy (SMA) have metabolic syndrome, and those who do tend to report worse life…
Survival outcomes in spinal muscular atrophy (SMA) are heavily influenced by age of onset, even among patients who are…
Use of the gene therapy Zolgensma (onasemnogene abeparvovec-xioi) was generally well tolerated and led to improvements in motor function…
A group of European experts has published updated recommendations for using the gene therapy Zolgensma (onasemnogene abeparvovec-xioi) in people…
The department of health (DoH) in Abu Dhabi — one of the seven emirates that make up the United Arab…
Most individuals with spinal muscular atrophy (SMA) type 2 experience improvements in physical abilities within a year after starting…
Twenty-six children were diagnosed with spinal muscular atrophy (SMA) in Russia through a 2022 pilot program, out of nearly…
Levels of certain molecules in cerebrospinal fluid (CSF) — the liquid that surrounds the brain and spinal cord — may…