My granddaughter is 3 yrs old type 2 and was diagnosed shortly after Spinraza was approved. She has had several treatments now and has seen significant gains. With new drugs being approved and studied, is there anyone looking at these in combination with Spinraza? I am in the r/d field so I have been doing my own investigating but so far have come up short of information regarding this.
Hey Scott, thanks for asking this. See Michael’s comment on your previous post, but I’d also recommend listening to the SMA News Today Podcast. We’ve addressed this topic there before, and I’m sure we’ll have more news to talk about in the coming months.
Like Michael said, it is all speculation at this point, but I do think pharmaceutical companies are looking into some sort of a combined therapy. For me personally, I’m content with Spinraza at the moment. But it will be interesting to see what kind of developments happen with Risdiplam and other therapies.
Keep us updated on your granddaughter!
Viewing 1 reply thread
You must be logged in to reply to this topic.
FDA Approves ZOLGENSMA for SMA! Talk about it now — click below:
SMA News Today is strictly a news and information website about the disease. It does not provide medical advice, diagnosis or treatment. This content is not intended to be a substitute for professional medical advice, diagnosis, or treatment. Always seek the advice of your physician or other qualified health provider with any questions you may have regarding a medical condition. Never disregard professional medical advice or delay in seeking it because of something you have read on this website.