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Do you have questions about risdiplam?
With the first-ever oral drug of its kind, risdiplam is sure to open new doors for the SMA community. This especially holds true for those who have spinal fusions and are unable to get Spinraza administered as a result.
Would you like to know more about risdiplam? If so, please send us your questions so that we can try to help you.
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2 Replies
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What are the benefits expected for older adults with SMA 2 (50+ years)?
Do you have to take it every day for the rest of your life?
What is the expected cost?
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All excellent questions, Tracy! I’m curious to know these answers, too.
With the drug currently under review, the FDA limits the amount of information the pharmaceutical company is allowed to release. Right now, the only concrete information we know is that Roche/Genentech has received priority review status, and this priority review status gives a good indication of the success of the clinical trials. But until the FDA actually grants Roche/Genentech approval for risdiplam, it’s probably more speculation than fact.
When more information becomes available, we will be sure to inform our forum members as soon as possible!
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