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  • The Morale Monologue #31 – EXCITING NEWS – Zolgensma Update – A MUST SEE

    Posted by michael-morale on September 4, 2019 at 7:10 am

    https://youtu.be/ihSVgTq76D0

    In this episode of the Morale Monologue, I’m sharing some information that was recently announced during the Cure SMA webinar, that was held on Wednesday, August 28, 2019. In this webinar, Cure SMA had representatives from AveXis Pharmaceuticals and the FDA. They discussed the most recent information regarding Zolgensma, along with information regarding the possibility of it becoming available to those of us that are adults.

    STRONG (NCT03381729) in SMA Type 2 children 6 months to 5 years

    REACH (NCT04042025) Possibly for adults up to 60 years

        * Est. Study Start Date:  09/01/2019

        * Est. Primary Completion Date:  12/31/2034

        * Est. Study Completion Date:  12/31/2034

    NOTE: The completion dates are for the conclusion of the REACH trial to end, but it may be available for SMA patients in 2022 or 2023

    For More Information:  http://www.clinicaltrials.gov

    deann-r replied 4 years, 9 months ago 2 Members · 1 Reply
  • 1 Reply
  • deann-r

    Member
    September 4, 2019 at 10:33 am

    Interesting info!

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