Tagged: avexis, avxs-101, Clinical trial, gene therapy, SMA treatment, SMA type 1, zolgensma This topic has 1 reply, 2 voices, and was last updated 3 years, 1 month ago by Ryan Berhar. Viewing 1 reply thread Author Posts April 30, 2019 at 3:00 pm #18609 Kevin SchaeferKeymaster This article summarizes the results of Zolgensma’s phase 3 trial. You can read all about it here: https://smanewstoday.com/2019/04/22/zolgensma-defying-sma-type-1-natural-history-in-str1ve-helping-treated-babies-to-breathe-and-sit-early-data-show/. Are any of you looking into Zolgensma? This question applies more to parents, but I’m curious to see if it’s something you’ve talked about with a medical specialist. April 30, 2019 at 8:17 pm #18634 Ryan BerharMember I hope it eventually becomes available for adults! Author Posts Viewing 1 reply thread You must be logged in to reply to this topic. Log In Username: Password: Keep me signed in Log In