By the time I was 19, I believed I had escaped my reproductive cycle. In fact, I had developed a superiority complex about it. While my friends complained about cramps and cravings, I laughed in their faces. It’s not like I was reading studies on young women with…
Scholar Rock has resubmitted its application seeking approval in the U.S. of its muscle-strengthening agent apitegromab — rejected last year due to manufacturing issues — for the treatment of children and adults with spinal muscular atrophy (SMA). The drug developer said it expects the U.S. Food and…
Discussion
A sick feeling sank like a rock in my stomach. My wheelchair would not fit in the airplane cargo hold, the airline employee told me. My only options were to refund our tickets or reroute us through another airline. My caregiver and I sat there, surrounded by our carry-on bags…
The U.S. Food and Drug Administration (FDA) has approved a high-dose regimen of Spinraza (nusinersen) — one that allows patients to receive consistently higher doses of the therapy after a shorter initial treatment loading phase — for spinal muscular atrophy (SMA). The new dosing regimen is authorized for use…
Discussion
Nearly anyone that knows me knows that pasta has been my lifelong favorite food. We stock a variety of shapes and flavors in the pantry so I always have different options to choose from. Among them are single serving, microwaveable mac ‘n cheese cups. A few weeks ago, I realized…
Children with spinal muscular atrophy (SMA) showed trends suggesting that nutritional status may be linked to motor function, according to a study in Poland that tracked 38 children over one year. Researchers found that increases in BMI — a measure…
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