Michael Discusses Possible Combination Therapy for SMA

[lupa-f]

I’m skeptical of any muscle targeted treatments having any lasting effects because SMA is not a muscle disease, it’s a neurological disease. If it were a muscle disease there are things already available that help build muscle like steroids that should help, but they don’t.

If they find a way to help regenerate motor neurons that would certainly be effective, but it doesn’t seem like there’s anything close on that front.

[pamela-muhammad]

I am hopeful always because that is my nature. But I don’t want anything that is painful or has too many dangerous side effects, if th that’s  the case I would rather just deal with SMA. But I am open minded. Thank you for sharing.