Scholar Rock and SRK 015 - EXCITING NEW POTENTIAL TREATMENT FOR SMA

A father’s perspective: Our journey to finding a treatment

When Quinn, our soon-to-be-born daughter, didn’t make as much movement in the womb as our other 3 children, my wife, Annie, and I thought we had the “chillest” baby in the world. We joked that she was saving up all her energy for when she entered this world kicking and screaming. Quinn was born in August 2018, and she was the most beautiful little girl. Over the first few months, nothing seemed out of the ordinary. In fact, she appeared healthy and had strong upper body strength. But by the time Quinn’s 9-month check-up came around in June, her physical condition started to change.

This topic has 2 replies, 2 voices, and was last updated 2 months, 2 weeks ago by Alyssa Silva.

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- March 18, 2020 at 7:55 am #22756
  Michael Morale
  Keymaster
  In this episode of the Morale Monologue, I’m discussing another biopharmaceutical company by the name of Scholar Rock, and their potential treatment known as SRK-015. I discuss how SRK-015 impacts our body, and how it differs from Spinraza, Zolgensma and risdiplam. While it may be over a year before this potential treatment gets approved by the FDA, it’s still proof that pharmaceutical companies are making advancements toward new treatments for those of us who suffer from spinal muscular atrophy.
  - SRK-015 Data Continue to Support Potential for SMA, Scholar Rock Says: https://smanewstoday.com/2020/02/21/srk-015-data-continue-to-support-potential-for-sma-scholar-rock-says/
  - Early Data Support SRK-015 Development for SMA Types 2–3, Scholar Rock Says: https://smanewstoday.com/2019/10/09/early-data-support-srk-015-development-for-sma-types-2-3-scholar-rock-says/
  - Scholar Rock Announces Additional Preclinical Data Supporting SRK-015 as Potential SMA Treatment: https://smanewstoday.com/2018/11/30/additional-preclinical-data-supports-srk-015-as-potential-sma-treatment/
- March 18, 2020 at 9:25 am #22761
  
  DeAnn R
  Keymaster
  
  I do remember hearing about this one a while back. Thanks for the great info!
- March 18, 2020 at 9:37 am #22762
  
  Alyssa Silva
  Keymaster
  
  I’ve had my eye on this drug for a while. Thinking it’d be a good cocktail with Spinraza. Happy to see things moving in the right direction.
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