• Growing Pains Can Be a Real Headache with SMA
  • Cytokinetics to Present Latest Updates on Therapy Candidate at Cure SMA Conference
  • Cure SMA Pursues More Education and Better Clinical Trial Access, Capacity
  • AveXis’ Gene Therapy AVXS-101 Edges Closer to Pivotal Trial for SMA Type 1
  • Daddy’s Bunny Suit Helps the Spinraza Go Down
  • Post-College Career Finds the Bright Side of a Broken System
  • The Aftermath of My Amtrak Residency Trip, Part 1
  • UK’s SMA Trust Determined to Fund Research, Bring New Treatments to Patients
  • Ready for the Rain: Quick Action Saves the Day
  • Campaign to Persuade States to Screen Newborns for SMA to Be Key Topic at Conference
  • Do I Hate It when People Tell Me that I’m an Inspiration?
  • The Train Rides End and the Great Work Begins